To evaluate the safety (acute effects associated with infusions, and inhibitor development),
pharmacokinetics (PK), and efficacy with respect to breakthrough bleeding during prophylaxis
and with respect to control of hemorrhaging in both the prophylaxis and on demand groups of
IB1001 in subjects with hemophilia B.
Minimum age: 5 Years.
Maximum age: N/A.
Gender(s): Male.
Hopital Edouard Herriot, Lyon 69437, France
Ospedale di Careggi, Florence I-50134, Italy
University of Milan, Milano I-20122, Italy
MTZ Clinical Research, Warsaw 02-106, Poland
City of Hope, Duarte, California 91010, United States
The Hemophilia Treatment Center of Orthopaedic Hospital, Los Angeles, California 90007, United States
Royal Free Hospital, London, England NW3 2QG, United Kingdom
Manchester Haemophilia Comprehensive Care Manchester Royal Infirmary, Manchester, England M13 9WL, United Kingdom
Royal Hallamshire Hospital, Sheffield, England S102JF, United Kingdom
Emory University School of Medicine Pediatric Hematology, Atlanta, Georgia 30322, United States
Centre for Haemostasis and Thrombosis, Basingstoke and North Hampshire Foundation Trust, Basingstoke, Hampshire RG24 9NA, United Kingdom
Rush University Medical Center-Pediatric Hematology Oncology, Chicago, Illinois 60612, United States
Indiana Hemophilia & Thrombosis Center, Indianapolis, Indiana 46260, United States
Centre Regional de Traitement de l 'Hemophilie, Nantes, Loire-Atlantique 44093, France
Jehangir Clinical Development Centre, Pune, Maharashtra 411 011, India
Sahyadri Specialty Hospital, Deccan Gymkhana, Pune, Maharashtra 411 004, India
University of Minnesota Center for Bleeding and Clotting Disorder, Minneapolis, Minnesota 55455, United States
Hemophilia Treatment Center of Las Vegas, Las Vegas, Nevada 89109, United States
Hemophilia and Thrombosis Center, Cincinnati, Ohio 45229, United States
The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, United States
The National Hemophilia Center-Sheba MC, Tel Hashomer, Ramat Gan 52621, Israel
University of Texas Health Science Center-Houston, Gulf States Hemophilia & Thrombophilia Center, Houston, Texas 77030, United States
University Hospital of Wales Health Park, Cardiff, Wales CF4 4XN, United Kingdom