The aim of this study is to describe Health Related Quality of Life (HRQoL) in adolescents
and adults with Hemophilia A treated prophylactically or on-demand with Helixate NexGen. The
study will also assess the kinds of determinants, including key transitional life events,
that might impact HRQoL in this patient population.
Minimum age: 14 Years.
Maximum age: 35 Years.
Gender(s): Male.
Inclusion Criteria:
- Haemophilia A patient
- Severely (<1%) and moderately (1-5%) affected
- On treatment with Helixate NexGen
- Ability to read and understand study materials (patient information and data
protection form, patient-related questionnaires)
- Signed data protection form; if patient is <18 years of age, legal guardian must also
give written consent by signing the data protection form
Exclusion Criteria:
- Presence of inhibitors
- Abuse of recreational drugs or alcohol interfering with the every-day-life in the
opinion of the physician
- Advanced stage human immunodeficiency virus (HIV) infection (CD4 cell counts
<200/cmm, multi-drug resistance, presence of AIDS related signs or symptoms)
- Symptomatic liver disease (cirrhosis, ascites, esophageal varices)
- Concomitant or planned interferon therapy
- Malignancies on or off treatment
CSLB Study Site 22, Graz, Austria
CSLB Study Site 26, Grieskirchen, Austria
CSLB Study Site 24, Innsbruck, Austria
CSLB Study Site 29, Klagenfurt, Austria
CSLB Study Site 23, Linz, Austria
CSLB Study Site 25, St. Pölten, Austria
CSLB Study Site 20, Vienna, Austria
CSLB Study Site 21, Vienna, Austria
CSLB Study Site 27, Vienna, Austria
CSLB Study Site 52, Edegem, Belgium
CSLB Study Site 51, Leuven, Belgium
CSLB Study Site 65, Amiens, France
CSLB Study Site 68, Poitiers Cedex, France
CSLB Study Site 60, Rouen, France
CSLB Study Site 64, Strasbourg, France
CSLB Study Site 66, Valence, France
CSLB Study Site 1, Berlin, Germany
CSLB Study Site 3, Bonn, Germany
CSLB Study Site 2, Bremen, Germany
CSLB Study Site 6, Delmenhorst, Germany
CSLB Study Site 7, Göttingen, Germany
CSLB Study Site 4, München, Germany
CSLB Study Site 72, Genova, Italy
CSLB Study Site 71, Milan, Italy
CSLB Study Site 74, Napoli, Italy
CSLB Study Site 73, Palermo, Italy
CSLB Study Site 98, Badajoz, Spain
CSLB Study Site 95, Jaen, Spain
CSLB Study Site 91, Valencia, Spain
CSLB Study Site 35, St. Gallen, Switzerland
CSLB Study Site 36, Zürich, Switzerland