Myozyme Related Published Studies
Well-designed clinical trials related to Myozyme (Alglucosidase Alfa)
A randomized study of alglucosidase alfa in late-onset Pompe's disease. [2010.04.15]
Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease. [2009.09]
Well-designed clinical trials possibly related to Myozyme (Alglucosidase Alfa)
Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease. [2007.01.09]
Other research related to Myozyme (Alglucosidase Alfa)
High antibody titer in an adult with Pompe disease affects treatment with alglucosidase alfa. [2010.12]
Enzyme replacement therapy with alglucosidase alfa in 44 patients with late-onset glycogen storage disease type 2: 12-month results of an observational clinical trial. [2010.01]
A randomized study of alglucosidase alfa in late-onset Pompe's disease. [2010]
Desensitization of an adult patient with Pompe disease and a history of anaphylaxis to alglucosidase alfa. [2009.11]
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. [2009.03]
Phenotype variations in early onset Pompe disease: diagnosis and treatment results with Myozyme. [2009]
Other possibly related research studies
Infantile-onset Pompe disease: a diagnosis not to miss. [2010.04]
Prognostic factors for the late onset Pompe disease with enzyme replacement therapy: from our experience of 4 cases including an autopsy case. [2010.05]
Enzyme replacement therapy for infantile Pompe disease during the critical period and identification of a novel mutation. [2009.12]
Pompe disease in infants: improving the prognosis by newborn screening and early treatment. [2009.12]
[Pompe's disease--part II. Treatment strategies and enzyme replacement] [2009.09.30]
Glycoengineered acid alpha-glucosidase with improved efficacy at correcting the metabolic aberrations and motor function deficits in a mouse model of Pompe disease. [2009.06]
Glycogen storage disease type II (Pompe disease)--influence of enzyme replacement therapy in adults. [2009.02]
Pompe disease: a neuromuscular disease with respiratory muscle involvement. [2009.04]
Therapeutic approaches in glycogen storage disease type II/Pompe Disease. [2008.10]
Improvement with ongoing Enzyme Replacement Therapy in advanced late-onset Pompe disease: a case study. [2008.12]
Arrhythmias in patients receiving enzyme replacement therapy for infantile Pompe disease. [2008.10]
Enzyme replacement therapy in severe adult-onset glycogen storage disease type II. [2008.08]
Report of the first Brazilian infantile Pompe disease patient to be treated with recombinant human acid alpha-glucosidase. [2008.05]
Immune tolerance induction to enzyme-replacement therapy by co-administration of short-term, low-dose methotrexate in a murine Pompe disease model. [2008.04]
[New approaches for the treatment of metabolic myopathies] [2007.10]
Enhanced response to enzyme replacement therapy in Pompe disease after the induction of immune tolerance. [2007.11]
[Enzyme replacement therapy in a patient with Pompe disease] [2007.09]
[Enzyme replacement therapy in Pompe's disease] [2007.07.15]
Cardiac arrhythmias following anesthesia induction in infantile-onset Pompe disease: a case series. [2007.08]
Differential muscular glycogen clearance after enzyme replacement therapy in a mouse model of Pompe disease. [2007.08]
Fractures in children with Pompe disease: a potential long-term complication. [2007.05]
Glycogen storage disease types I and II: treatment updates. [2007.04]
Acid alpha-glucosidase deficiency (Pompe disease). [2007.01]
Pompe's disease. [2008.10.11]
24-months results in two adults with Pompe disease on enzyme replacement therapy. [2011.06]
Oral administration of recombinant human acid alpha-glucosidase reduces specific antibody formation against enzyme in mouse. [2011.05]
Pompe disease: from new views on pathophysiology to innovative therapeutic strategies. [2011.06]
Adult Pompe disease: clinical manifestations and outcome of the first Greek patients receiving enzyme replacement therapy. [2011.05]
[Enzyme replacement therapy of lysosomal storage diseases]. [2010.12]
Late form of Pompe disease with glycogen storage in peripheral nerves axons. [2011.02.15]
Use of cardiac magnetic resonance imaging to evaluate cardiac structure, function and fibrosis in children with infantile Pompe disease on enzyme replacement therapy. [2010.12]
Differences in the predominance of lysosomal and autophagic pathologies between infants and adults with Pompe disease: implications for therapy. [2010.12]
Pompe disease: dramatic improvement in gastrointestinal function following enzyme replacement therapy. A report of three later-onset patients. [2010.10]
Hearing loss in Pompe disease revisited: results from a study of 24 children. [2010.10]
Oropharyngeal dysphagia in infants and children with infantile Pompe disease. [2010.12]
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